Cell and Gene Therapy in Rare Disorders Market Size, Share, Report, and Forecast 2024-2032

1 EXECUTIVE SUMMARY
2 MARKET INTRODUCTION
2.1 DEFINITION
2.2 SCOPE OF THE STUDY
2.3 RESEARCH OBJECTIVE
2.4 MARKET STRUCTURE
3 RESEARCH METHODOLOGY
3.1 OVERVIEW
3.2 DATA FLOW
3.2.1 Data Mining Process
3.3 PURCHASED DATABASE:
3.4 SECONDARY SOURCES:
3.4.1 Secondary Research data flow:
3.5 PRIMARY RESEARCH:
3.5.1 Primary Research DATA FLOW:
3.5.2 Primary Research: Number of Interviews conducted
3.5.3 Primary Research: Regional Coverage
3.6 APPROACHES FOR MARKET SIZE ESTIMATION:
3.6.1 Revenue Analysis Approach
3.7 DATA FORECASTING
3.7.1 Data forecasting Type
3.8 DATA MODELING
3.8.1 microeconomic factor analysis:
3.8.2 Data modeling:
3.9 TEAMS AND ANALYST CONTRIBUTION
4 MARKET DYNAMICS
4.1 INTRODUCTION
4.2 DRIVERS
4.2.1 Growing incidences of Cancer and rare disorders
4.2.2 Increasing approval for Gene and Cell therapy Products
4.3 RESTRAINTS
4.3.1 Clinical Trial Failure associated with gene and cell therapy
4.4 OPPORTUNITY
4.4.1 Growing investment in the field of gene and cell therapy
5 MARKET FACTOR ANALYSIS
5.1 PORTER'S FIVE FORCES MODEL
5.1.1 Threat of New Entrants
5.1.2 BARGAINING POWER OF SUPPLIERS
5.1.3 Threat of Substitutes
5.1.4 Bargaining Power of Buyers
5.1.5 Intensity of Rivalry
5.2 IMPACT OF COVID-19 ON THE GLOBAL CELL AND GENE THERAPY MARKET
6 GLOBAL CELL AND GENE THERAPY MARKET, BY THERAPY TYPE
6.1 OVERVIEW
6.2 CELL THERAPY
6.2.1 Autologous
6.2.2 Allogeneic
6.3 GENE THERAPY
6.3.1 Ex vivo
6.3.2 In vivo
7 GLOBAL CELL AND GENE THERAPY MARKET, BY APPLICATION
7.1 OVERVIEW
7.2 CANCER
7.3 NEUROLOGICAL DISORDERS
7.4 CARDIOVASCULAR DISORDERS
7.5 RARE DISEASES
7.6 OPHTHALMOLOGY
7.7 BLOOD DISORDERS
7.8 OTHERS
8 GLOBAL CELL AND GENE THERAPY MARKET, BY REGION
8.1 OVERVIEW
8.2 NORTH AMERICA
8.2.1 US
8.2.2 CANADA
8.3 EUROPE
8.3.1 Germany
8.3.2 France
8.3.3 UK
8.3.4 Italy
8.3.5 Spain
8.3.6 Rest of Europe
8.4 ASIA-PACIFIC
8.4.1 China
8.4.2 India
8.4.3 Japan
8.4.4 Australia
8.4.5 South Korea
8.4.6 Rest of Asia-pacific
8.5 REST OF THE WORLD
8.5.1 Middle East & Africa
8.5.2 South America
9 COMPETITIVE LANDSCAPE
9.1 INTRODUCTION
9.2 MARKET SHARE ANALYSIS, 2022
9.3 COMPETITOR DASHBOARD
9.4 PUBLIC PLAYERS STOCK SUMMARY
9.5 COMPARATIVE ANALYSIS: KEY PLAYERS FINANICAL
9.6 KEY DEVELOPMENTS & GROWTH STRATEGIES
9.6.1 product launch / Product approval
9.6.2 Collaboration
9.6.3 Agreement
9.6.4 Expansion
10 COMPANY PROFILES
10.1 NOVARTIS AG
10.1.1 COMPANY OVERVIEW
10.1.2 FINANCIAL OVERVIEW
10.1.3 products OFFERED
10.1.4 KEY DEVELOPMENTS
10.1.5 SWOT ANALYSIS
10.1.6 KEY STRATEGIES
10.2 BRISTOL-MYERS SQUIBB COMPANY
10.2.1 COMPANY OVERVIEW
10.2.2 FINANCIAL OVERVIEW
10.2.3 products OFFERED
10.2.4 KEY DEVELOPMENTS
10.2.5 SWOT ANALYSIS
10.2.6 KEY STRATEGIES
10.3 AMGEN INC.
10.3.1 COMPANY OVERVIEW
10.3.2 FINANCIAL OVERVIEW
10.3.3 productS OFFERED
10.3.4 KEY DEVELOPMENTS
10.3.5 KEY STRATEGIES
10.4 AURION BIOTECH
10.4.1 COMPANY OVERVIEW
10.4.2 FINANCIAL OVERVIEW
10.4.3 productS OFFERED
10.4.4 KEY DEVELOPMENTS
10.4.5 KEY STRATEGIES
10.5 SAREPTA THERAPEUTICS, INC.
10.5.1 COMPANY OVERVIEW
10.5.2 FINANCIAL OVERVIEW
10.5.3 productS OFFERED
10.5.4 KEY DEVELOPMENTS
10.5.5 KEY STRATEGIES
10.6 FERRING B.V.
10.6.1 COMPANY OVERVIEW
10.6.2 FINANCIAL OVERVIEW
10.6.3 products OFFERED
10.6.4 KEY DEVELOPMENTS
10.6.5 SWOT ANALYSIS
10.6.6 KEY STRATEGIES
10.7 SIBIONO GENETECH CO. LTD., SHENZHEN (SIBIONO)
10.7.1 COMPANY OVERVIEW
10.7.2 products OFFERED
10.7.3 KEY DEVELOPMENTS
10.7.4 KEY STRATEGIES
10.8 BLUEBIRD BIO, INC.
10.8.1 COMPANY OVERVIEW
10.8.2 FINANCIAL OVERVIEW
10.8.3 PRODUCTS OFFERED
10.8.4 KEY DEVELOPMENTS
10.8.5 SWOT Analysis
10.8.6 KEY STRATEGIES
10.9 KITE PHARMACEUTICALS, INC.
10.9.1 COMPANY OVERVIEW
10.9.2 FINANCIAL OVERVIEW
10.9.3 PRODUCTS OFFERED
10.9.4 KEY DEVELOPMENTS
10.9.5 SWOT Analysis
10.9.6 KEY STRATEGIES
10.10 JANSSEN GLOBAL SERVICES
10.10.1 COMPANY OVERVIEW
10.10.2 FINANCIAL OVERVIEW
10.10.3 Products OFFERed
10.10.4 KEY DEVELOPMENTS
10.10.5 KEY STRATEGIES
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